Duchenne muscular dystrophy's impact on the brain may be reversible
New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...
PTC Therapeutics says EC will not renew market authorization for muscle disorder drug
PTC Therapeutics said on Friday its inherited progressive muscle-wasting disorder drug will no longer be available for sale in the EU as the European Commission has decided not to renew its marketing ...
European Commission Declines To Renew Marketing Authorization Of Translarna Duchenne Muscular Disorder
PTC Therapeutics' Translarna loses EU conditional approval, but countries may allow continued use. PTC submitted four FDA ...
PTC Therapeutics says EC not to renew market authorization for muscle disorder drug
PTC Therapeutics said on Friday its inherited progressive muscle-wasting disorder drug will no longer be available for sale in the EU as the European Commission has decided not to renew its ...
SMA News Today23h
MDA 2025: Spinraza treatment stabilizes adult motor function
Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...