An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

Study results support the role of functional dystrophin and suggest that delandistrogene moxeparvovec stabilizes or slows ...

Ifetroban demonstrated significant 5.4% improvement in cardiac functionNASHVILLE, Tenn., March 19, 2025 /PRNewswire/ -- Cumberland Pharma ...

The company plans to submit a biologics licence application to the US Food and Drug Administration later this year.

A young man treated with Elevidys died of acute liver failure. The case may give doctors pause before prescribing the ...

Multiparametric quantitative MRI could potentially help differentiate between Duchenne muscular dystrophy and Becker muscular ...

The Phase I/II Deliver trial sought to establish the impact of DYNE-251 on several mobility-related endpoints, seeing an ...

The parents of an eight-year-old boy with Duchenne muscular dystrophy are pleading with doctors to give their son a drug that will prolong his life.

Sam Millar from Edinburgh, was diagnosed with Duchenne muscular dystrophy, a disease that leads to loss of ... so that Sam ...

Sam Millar, eight, was diagnosed with Duchenne muscular dystrophy with his parents told there was a life-changing drug that ...

A comprehensive care approach can help people with ambulatory DMD maximize function and retain the ability to walk for as ...