Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...

Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

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The health activists argue that the government is empowered with effective law and policy tools and therefore should ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Scholar Rock (SRRK), a late-stage biopharmaceutical company developing innovative treatments for spinal muscular atrophy, ...

KOCHI: Residents of Cherai are rallying to support two-and-a-half-year-old Adharv, who is suffering from Spinal Muscular ...

Kate Middleton joked about her “huge” hands as she left her print on the wall of the Ty Hafan children’s hospice in South ...

Diana helped to kickstart fundraising for the hospice in 1995, with Luciano Pavarotti performing a concert at Castle Castle to raise money for the charity at the Princess' request. Tŷ Hafan opened its ...

Princess Kate played with seriously ill children and chatted with bereaved families on a surprise visit to Wales on Thursday.