Congenital heart disease (CHD) is one of the most common birth defects, but the full extent of its genetic underpinnings has ...

Genetic engineering in non-human primates has long been limited by the need for virus-based gene delivery methods. Recently, researchers in Japan successfully used a nonviral system to introduce a ...

Cedars-Sinai investigators have developed a novel artificial intelligence (AI) model, named DYNA, that accurately ...

The goal of genome editing technology is to develop strategies for the correction of those mutations that are responsible of ...

Scientists say they have identified a potential new gene target that could be edited to treat sickle cell disease, an ...

Scientists at deCODE genetics, a subsidiary of Amgen, reveal today in Nature Genetics associations between bipolar disorder and rare loss-of-function variants in two genes.

Tenaya Therapeutics (TNYA) announced the publications of positive preclinical data for TN-201, the company’s gene therapy candidate for Myosin-Binding Protein C3-associated hypertrophic cardiomyopathy ...

Resilience relies on the brain’s ability to regulate emotion, adapt, and recover. Myelin plasticity helps speed up and stabilize resilient brain responses. Genes like FKBP5 and BDNF affect how people ...

New research has provided insight into the biological mechanisms that may contribute to poor outcomes in certain cases of ...

Epilepsy researcher Sujithra Srinivas discusses the value of translational research for understanding and treating neurologic ...

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