The goal of genome editing technology is to develop strategies for the correction of those mutations that are responsible of ...
The U.S. Food and Drug Administration approved Soleno Therapeutics' drug to treat a rare genetic disorder on Wednesday, ...
In a manuscript published in the American Journal of Psychiatry titled "Psychiatric Genetics in Clinical Practice: Essential ...
Base editing corrected a mutation that causes macular degeneration, highlighting the potential of gene therapy to treat ...
Genetic engineering in non-human primates has long been limited by the need for virus-based gene delivery methods. Recently, ...
Affecting 1 in 500 people, hypertrophic cardiomyopathy is a condition in which the walls of the left ventricle, the heart's ...
Japanese researchers used a nonviral piggyBac system to genetically modify cynomolgus monkeys, enabling more accurate disease ...
Genetic engineering in non-human primates has long been limited by the need for virus-based gene delivery methods. Recently, ...
Noninvasive Measurement of Gene Expression at Target Locations in ... of the muscles of those affected by this inherited genetic disease, but perhaps, in ... With Gene Editing, Mice With a Form ...
Congenital heart disease (CHD) is one of the most common birth defects, but the full extent of its genetic underpinnings has ...
A team of researchers at Karolinska Institutet has developed a novel tool for genetic research. The study, published in ...
Advances in the gene-editing technology known as CRISPR-Cas9 over the past 15 years have yielded important new insights into the roles that specific genes play in many diseases. But to date this ...