Solid Biosciences Inc. (Nasdaq: SLDB), a life sciences company developing precision genetic medicines for neuromuscular and ...
Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in the ...
Multiparametric quantitative MRI could potentially help differentiate between Duchenne muscular dystrophy and Becker muscular ...
Duchenne muscular dystrophy (DMD) is a genetic condition ... carries the condition won’t show many — or possibly any — symptoms because they have a second, functional copy of the gene.
Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in the ...
A young man treated with Elevidys died of acute liver failure. The case may give doctors pause before prescribing the ...
Duchenne muscular dystrophy (DMD) is a severe and progressive ... soon as possible and can also teach you what warning signs and symptoms to watch for when you’re on your own.
The parents of an eight-year-old boy with Duchenne muscular dystrophy are pleading with doctors to give their son a drug that will prolong his life.
Duchenne muscular dystrophy (DMD ... DMD is one of the most severe forms of muscular dystrophy, with symptoms worsening quickly. Symptoms appear in early childhood. There is currently no cure ...
Italfarmaco S.p.A. today announced a comprehensive update on the regulatory and clinical advancements for givinostat, the company’s drug for the treat ...