Organoids were cultured from healthy donor iPSC sources and differentiated using the human iPSC-derived Cerebral Organoid ...

Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...

(MENAFN- EIN Presswire) Leading Pharmaceutical companies are advancing the AAV vector gene therapy pipeline and its future growth potential. LAS VEGAS , NV, UNITED STATES, February 7, 2025 ...

Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.

Researchers have demonstrated, for the first time in the world using mice, the ability to overcome significant challenges in ...

The candidate in question is VY9323, an AAV gene therapy combining a highly potent pri-miRNA against superoxide dismutase 1 ...

Viralgen and the CTNNB1 Foundation have come together to manufacture an investigational gene therapy designed to treat CTNNB1 ...

Gene editing is already being used to treat a handful of rare genetic diseases; however, most therapies involve breaking or ...

Astellas has invested heavily in novel technologies that are not necessarily the most successful or popular in the industry.

Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...

The nano-complexes released the loaded-AAV intracellularly ... approach to viral vector treatments, which are currently limited by neutralizing antibodies. Gene therapy is a treatment method ...

Patients with CTNNB1 Syndrome will benefit from this joint effort to develop and manufacture a new AAV investigational gene therapy ... a clinically validated vector that is expected to enter ...