An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

A young man treated with Elevidys died of acute liver failure. The case may give doctors pause before prescribing the ...

Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in the ...

A comprehensive care approach can help people with ambulatory DMD maximize function and retain the ability to walk for as ...

Sarepta Therapeutics said that a young man died after receiving Elevidys, its gene therapy for Duchenne muscular dystrophy ...

Surveys of caregivers and health care providers reveal gaps in screening and management of neuropsychiatric and neurodevelopmental symptoms among patients with Duchenne muscular dystrophy in the ...

A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...

A young man with Duchenne MD and treated with Elevidys has died of acute liver failure, Sarepta reports; it's working with ...

The parents of an eight-year-old boy with Duchenne muscular dystrophy are pleading with doctors to give their son a drug that will prolong his life.

The Minnesota Department of Health tests for over 60 different disorders during a newborn screening, and now, two more ...

Multiparametric quantitative MRI could potentially help differentiate between Duchenne muscular dystrophy and Becker muscular dystrophy early and improve the management of these conditions.

Solid Biosciences Inc. (Nasdaq: SLDB), a life sciences company developing precision genetic medicines for neuromuscular and ...