New gene therapy cures 1st New Yorker of sickle cell anemia

Sickle cell anemia patient reunites with Long Island doctors whose gene therapy treatments made him symptom-free
Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy.
Long Island patient gets breakthrough sickle cell treatment called a ‘cure’: ‘I’m not in pain anymore’
He’s got new blood. A Long Island hospital said it administered life-changing Lyfgenia gene therapy treatment and successfully wiped away sickle cell disease from a Laurelton man. Cohen Children’s Medical Center said patient Sebastien Beauzile,
Gene therapy cures man from sickle cell
A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life. He was Sebastien Beauzile was born with sickle cell anemia and struggled to live a pain free life. However,
‘I’m Unstoppable’: New gene therapy cures first New Yorker of sickle cell anemia
Twenty-one-year-old Sebastien Beauzile was all smiles as he was serenaded with “Happy Birthday” on what he calls his new birthday at Cohen Children’s Medical
Sickle cell gene therapy frees teen from life of pain
Aaron Scott, of Fayetteville, is the first in North Carolina to receive a new FDA-approved therapy which uses the patient's own cells to relieve the pain of sickle cell disease.
Man makes history by becoming the first in New York to be cured of sickle cell anemia, doctors say
A Long Island hospital has said that it has successfully eliminated sickle cell disease from Sebastien Beauzile, a 21-year-old from Laurelton, using the groundbreaking Lyfgenia gene therapy. Cohen Children’s Medical Center confirmed Beauzile as the first New Yorker to receive this life-changing treatment,
CASGEVY: NHS Approves First Sickle Cell Gene Therapy
Learn how CASGEVY, the first NHS-approved CRISPR gene therapy, treats sickle cell disease through a revolutionary genetic editing technique.
Man becomes first in New York to be cured of sickle cell
For 21 years, Sebastien Beauzile suffered chronic pain from debilitating sickle cell anemia and now he is making medical history. “Sickle cell was like a blockade for me - now it’s like a wall that I just jumped over,
Breakthrough treatments offer some sickle cell sufferers a cure, but barriers remain
Esther Nkemakolam runs her fingers through kinetic sand and sings a “Moana” song as UPMC Children’s Hospital nurse Taylor ...
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Pioneering the world’s first CRISPR medicine for sickle cell disease
When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters ...
Mutated DNA Restored to Normal in Gene Therapy Advance
The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...
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Rutgers Cancer Institute receives gene therapy treatment center designation
The Rutgers Cancer Institute recently became a designated gene therapy treatment center for sickle cell anemia and beta-thalassemia, joining a small group of medical centers that currently provide ...
CRISPR Therapeutics: An Uninspiring Start For Casgevy
CRISPR Therapeutics' stock faces challenges with slow Casgevy adoption and competition. See how CRSP stock remains a cautious ...